Care for children with haemophilia in the Czech Republic
Authors:
J. Blatný; P. Ovesná
Authors‘ workplace:
Institut biostatistiky a analýz, Lékařská fakulta Masarykovy univerzity, Brno
; Oddělení dětské hematologie, FN Brno a Lékařská fakulta Masarykovy univerzity, Brno
Published in:
Čes-slov Pediat 2017; 72 (3): 148-153.
Category:
Overview
Haemophilia is rare, though severe disease. Significant improvements in care of haemophilia since second half of 20th century changed it from the deadly disease to the well-controlled condition. In the Czech Republic, haemophilia care is overseen and guaranteed by the Czech National Haemophilia Programme (CNHP) – an association of all haemophilia treatment centres in the country.
Haemophilia treatment is complex and multidisciplinary. CNHP runs the registry recording all relevant data concerning haemophilia treatment nation-wide. There were 246 children with haemophilia registered in the Czech Republic in 2015. With the treatment provided, their median annual bleeding rate was three even for those with severe disease. All children are offered home therapy, and all, who need it, are on prophylaxis. No child has been infected with HIV or HCV viruses. Children with inhibitors are offered immune-tolerance treatment. Though the treatment of haemophilia in children is effective and safe in these days in the Czech Republic, risks associated with the disease should not be underestimated.
Key words:
haemophilia, inhibitors, bleeding, prophylaxis
Sources
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Labels
Haematology Neonatology Paediatrics General practitioner for children and adolescentsArticle was published in
Czech-Slovak Pediatrics
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